Patients
Rare diseases
At Santhera, we are passionate about providing treatment options for patients with rare diseases, specifically in the area of neuromuscular conditions – diseases that have a severe impact on the lives of affected individuals.
Our research
Our research on therapies in rare diseases is currently focused on developing treatment options for:
Neuromuscular Diseases
- Duchenne muscular dystrophy (DMD) is one of the most common and devastating types of muscular degeneration and results in progressive muscle weakness, starting at an early age. Learn more
- Becker muscular dystrophy (BMD) is a progressive muscle wasting disease similar to Duchenne muscular dystrophy (DMD) but usually milder.